Two years after the U.S. FDA approval of Aqneursa (levacetylleucine) in Niemann-Pick disease type C, Intrabio Inc.’s ...

IntraBio is on a roll with its expansion plans for chemically altered amino acid, Aqneursa. | IntraBio's streak of success in the rare neurological category continues, as the drugmaker racks up a ...

The FDA has approved Aqneursa (levacetylleucine) for ataxia in adult and pediatric patients with ataxia-telangiectasia weighing at least 15 kg.

IntraBio Inc., a leader in the discovery, development, and commercialization of novel therapies for rare and common neurodegenerative diseases, today announced that the U.S. Food and Drug ...

A Hartlepool woman living with a rare neurological condition says time is of the essence as she campaigns for access to a ...

The mother of two teenagers with Friedreich's Ataxia has said it is “absolutely brilliant news” that the HSE has decided to reimburse a drug that slows the disease’s progression.  Friedreich's Ataxia ...

Ataxia-telangiectasia (AT) is a rare autosomal recessive disorder associated with immunodeficiency and an increased risk of malignancy. We report a young child with AT and severe combined ...

MINNEAPOLIS, Sept. 25, 2025 /PRNewswire/ -- The National Ataxia Foundation (NAF) today announced the launch of The Science Guy: Back in the Lab for FA, a new educational campaign to raise awareness ...

Ataxia means the loss of coordination of body movements. Acute cerebellar ataxia is a disorder in children that causes a sudden loss of coordination. It is relatively prevalent in children, especially ...

Ataxia is a form of movement disorder. There is loss of balance and physical co-ordination leading to difficulty in walking normally. The Cerebellum of the brain is normally responsible for ...

Ataxia is the defect in normal movements like walking, speaking, eating swallowing etc. It is caused most commonly by damage to the brain stem or cerebellum that regulates movements. There are over 50 ...